Current Studies
Study 165-306
A Phase 3 Multi Center Study to Evaluate the Safety and Efficacy of Subcutaneous Injections of Pegvaliase in Adolescent Subjects (Ages 12-17) with Phenylketonuria Featuring an Open Label Randomized Two Arm (Active vs Diet Only Control) Design
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Indication
Phenylketonuria (PKU)
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Investigational Therapeutic
BMN 165
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Study Type
Phase 3
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Goal
Evaluate safety and efficacy of BMN 165 in adolescents with PKU when administered as an Induction/Titration and Maintenance dose regimen.
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Status
This study is currently recruiting participants
Study 165-305
A Phase 3, Open-Label, Multi-Center Study to Assess the Safety and Efficacy of BMN 165 in Japanese Subjects 18 Years of Age and Older With Phenylketonuria
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Indication
Phenylketonuria (PKU)
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Investigational Therapeutic
BMN 165
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Study Type
Phase 3
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Goal
The primary objective of the study is to evaluate the efficacy and safety of BMN 165 in Japanese subjects ≥ 18 years of age with PKU when administered as an Induction/Titration and Maintenance dose regimen.
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Status
This study is ongoing, but not recruiting participants.